Lung Disease and Its Affect on the Work of White Blood Cells in the LungsĮxploring the Utility of Hyperpolarized 129Xe MRI in Healthy Volunteers and Patients With Lung DiseaseĪssessment of Changes in a Novel Histological Activity Scale in Response to ARO-AAT Phase 1 study to assess the safety, PK and PD of INBRX-101 in adults with Alpha-1 (rhAAT-Fc)Įffects of different exercise training modalities in Alpha-1 Antitrypsin DeficiencyĪ Study of DCR-A1AT in Healthy Adult Volunteers and Patients With A1ATD-Associated Liver DiseaseĪlvelestat (MPH996) for the Treatment of ALpha-1 ANTitrypsin DeficiencyĪlpha-1 Antitrypsin (AAT) Enhances Islet Autograft Survival in Patients With Chronic PancreatitisĬOPD Exacerbation Blood and Urine Biomarkers Study Liver Disease in Patients with Alpha-1 Antitrypsin Deficiency Evaluation of the Efficacy and Safety of VX-864 in Subjects With the PiZZ Genotype